On the morning of March 20, eye surgeon Jason Comander injected viruses carrying lab-grown genes into the eyes of a boy whose vision had been gradually disappearing. If all goes as planned, the ...
Physician and molecular biologist Katherine High remembers sitting at a staff meeting of the gene therapy company Spark Therapeutics on November 15, 2018, waiting to hear from a guest speaker, when ...
A brave six-year-old girl has had her sight restored thanks to 'incredible' life-changing eye gene therapy on the NHS. Little Saffie Sandford, from Stevenage in Hertfordshire, has the rare inherited ...
From reproductive rights to climate change to Big Tech, The Independent is on the ground when the story is developing. Whether it's investigating the financials of Elon Musk's pro-Trump PAC or ...
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A gene therapy that can restore sight to people born with degenerative blindness has earned its creators one of science’s most prestigious prizes, often described by its Silicon Valley founders as the ...
A married couple who created the first approved gene therapy for blindness have been awarded one of the most advantageous prizes in science. Molecular biologist Jean Bennett and ophthalmologist Albert ...
Breakthrough Prize in Life Sciences Awarded to Jean Bennett, Katherine A. High and Albert Maguire; Stuart H. Orkin and Swee Lay Thein; Rosa Rademakers and Bryan Traynor LOS ANGELES, April 19, 2026 ...
Researchers at Case Western Reserve University have developed gene-carrying nanoparticles that home in on target cells and prevent vision loss in mice with a human form of Leber congenital amaurosis.
LUXTURNA has significant market potential due to the high unmet need for effective treatments in rare genetic conditions. With its FDA approval for specific mutations in the RPE65 gene, it offers hope ...
Accutane (13-cis-retinoic acid) is used to treat severe, scarring acne, but it can also cause vision problems. New work shows that this unfortunate side effect is caused by 13-cis-retinoic acid ...
Voretigene neparvovec-rzyl (VN) therapy partially restored electroretinogram (ERG) responses in some RPE65-related retinopathy patients, with sustained improvements over several years. The study ...