SpliceBio aims to begin a study testing its protein splicing gene therapy in the first half of 2025, now that the FDA has cleared its IND.

At ASH's annual meeting, a study showed the potential for this method to inform the next treatment after patients relapse on BCMA- or GPRC5D-targeted therapy.

A stem cell transplant added to Rituxan did not improve survival for MRD-negative MCL patients in their first remission ...

Imlunestrant by itself benefited those with ESR1 mutations but also had broad efficacy in ER-positive HER2-negative tumors when combined with a CDK4/6 inhibitor.

The study is designed to evaluate the safety, tolerability, and preliminary efficacy of ATX-559 in certain biomarker-selected cancer patients.

Researchers at the meeting reported on long-term activity of commercialized gene therapies and preliminary data on ...

The new Future Medicines Institute, based at Queen's University Belfast, is backed by government and industry.

The data suggest that multiple myeloma patients on Janssen's CAR T-cell therapy lived longer than on BMS's but experienced ...

In the Phase II ADVL1823 study, researchers evaluated Vitrakvi in children with newly diagnosed IFS and other solid tumors with NTRK fusions.

The firm is on track to launch the gene therapy for dystrophic epidermolysis bullosa, called Vyjuvek in the US, in Germany in Q2 2025.

The variant, present in the NFKB1 gene and common in the Aymara community, could help guide treatment decisions, researchers ...

Researchers founded Rarity PBC as a public benefit corporation that will license the IP and develop operations to potentially ...