After years of heartbreak, researchers have found an experimental treatment that can slow the progression of Huntington’s disease, according to early results from a small clinical trial ...

Stunning success in halting Huntington's disease with gene therapy offers new hope to those with the disorder—and potential advances against Parkinson's and Alzheimer's.

Share on Pinterest The new gene therapy showed promise by significantly slowing down Huntington’s disease. Santi Nuñez/Stocksy Huntington’s disease is a genetic brain disorder that causes symptoms ...

Woody Guthrie (1912–1967) was a well-known singer/songwriter with undiagnosed Huntington's disease (HD), born to a family burdened by undiagnosed HD. Guthrie’s mother, Nora, had the diseasse and was ...

A gene therapy injected into patients’ brains slowed progression of the disease by 75 percent, preliminary findings reported.

An exceptionally rare and fatal genetic disease may finally have a solution. Huntington’s Disease affects one in ten to twenty thousand Americans. The disease is a mixture of dementia and Parkinson’s, ...

In a study reported by Uniqure, which developed the experimental gene therapy, scientists found that it slowed progression of Huntington’s disease by 75% over three years. The study has not yet been ...

I cried with every single patient,” Sung says. “It just was this crazy feeling that, for the patients and families, almost can’t feel real.” The treatment, known as AMT-130, is delivered deep into the ...

New gene therapy offers hope for Huntington's disease, potentially increasing quality of life significantly. Trial results indicate a 75% reduction in disease progression after three years, showcasing ...

As well as slowing disease progression by 75 percent at 36 months, the scientists found that neurofilament light protein (NfL)—a biomarker of neuronal damage—levels in spinal fluid were lower in ...

The new therapy is being hailed as a breakthrough. But the small study has some limitations – and hasn’t been peer-reviewed.

Once thought impossible to treat, Huntington's disease has been successfully slowed by a breakthrough gene therapy. This costly but life-changing 18-hour brain surgery reportedly offers patients ...