After years of heartbreak, researchers have found an experimental treatment that can slow the progression of Huntington’s ...

Stunning success in halting Huntington's disease with gene therapy offers new hope to those with the disorder—and potential ...

A one-time gene therapy called AMT-130 helped slow the progression of Huntington's disease by 75%, paving the way for the ...

Stunning success in halting Huntington's disease with gene therapy offers new hope to those with the disorder—and promises ...

A gene therapy injected into patients’ brains slowed progression of the disease by 75 percent, preliminary findings reported.

An exceptionally rare and fatal genetic disease may finally have a solution. Huntington’s Disease affects one in ten to ...

In a study reported by Uniqure, which developed the experimental gene therapy, scientists found that it slowed progression of ...

I cried with every single patient,” Sung says. “It just was this crazy feeling that, for the patients and families, almost can’t feel real.” The treatment, known as AMT-130, is delivered deep into the ...

New gene therapy offers hope for Huntington's disease, potentially increasing quality of life significantly. Trial results ...

As well as slowing disease progression by 75 percent at 36 months, the scientists found that neurofilament light protein (NfL)—a biomarker of neuronal damage—levels in spinal fluid were lower in ...

The new therapy is being hailed as a breakthrough. But the small study has some limitations – and hasn’t been peer-reviewed.

The director of UVA’s treatment program sees reason for “cautious optimism” after a small study’s positive results.