Treatment introduces an expansion of the scope of gene therapies that might lead to similar treatments for neurodegenerative ...

French biotech EG 427 has had success with its urinary incontinence DNA therapy, EG110A, showing a more than 80% reduction in ...

Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct ...

A one-time gene therapy called AMT-130 helped slow the progression of Huntington's disease by 75%, paving the way for the ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the ...

Huntington’s disease has been successfully treated for the first time using a gene therapy, which may be available in the US ...

A gene-editing therapy led to durable changes in serum transthyretin levels among people with hereditary transthyretin ...

D Molecular Therapeutics (FDMT) offers attractive growth potential with strong cash reserves and promising late-stage gene ...

New gene therapy offers hope for Huntington's disease, potentially increasing quality of life significantly. Trial results ...

Stunning success in halting Huntington's disease with gene therapy offers new hope to those with the disorder—and potential ...

In a trial of people with early Huntington's, the newly developed therapy slowed the progression of symptoms by 75%.

A company called uniQure has announced promising results from a trial of a new gene therapy for Huntington's disease. The ...