Treatment introduces an expansion of the scope of gene therapies that might lead to similar treatments for neurodegenerative ...
Gene therapies for rare diseases are frequently developed then discarded by drug companies because they can’t afford to ...
In a study reported by Uniqure, which developed the experimental gene therapy, scientists found that it slowed progression of ...
French biotech EG 427 has had success with its urinary incontinence DNA therapy, EG110A, showing a more than 80% reduction in ...
After three patients died, the maker of an investigational gene therapy stopped shipments of the drug after it refused to ...
This sponsored article was provided by a partner and is not editorial content from Los Angeles Magazine or the Engine Vision Media Network. Every cell in your body holds a unique genetic code within ...
MedPage Today on MSN
Gene-Editing Therapy Promising for Rare Hereditary Disease
A gene-editing therapy led to durable changes in serum transthyretin levels among people with hereditary transthyretin ...
The Brighterside of News on MSN
AI-powered CRISPR technology turbocharges gene therapy development
Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct ...
A one-time gene therapy called AMT-130 helped slow the progression of Huntington's disease by 75%, paving the way for the ...
New Scientist on MSN
Huntington’s disease breakthrough: what to know about the gene therapy
An experimental gene therapy has become the first treatment to successfully slow the progression of Huntington’s disease. While the findings are still preliminary, the approach could be a major ...
The FDA has granted Fast Track designation to SAR446268 for the treatment of non-congenital myotonic dystrophy type 1.
Some results have been hidden because they may be inaccessible to you
Show inaccessible results