Bayer's pioneering cell and gene therapies for Parkinson's disease are at the forefront of an exciting but risky test of CEO ...

At the European Cell & Gene Therapy Summit 2025, funding challenges and innovation drove discussions on the sector’s future.

Three draft recommendation documents published on Wednesday are intended to guide drug sponsors and accelerate the ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the ...

Exagamglogene autotemcel (exa-cel), a CRISPR/Cas9 gene-edited cell therapy, eliminated vaso-occlusive crises in 97% of ...

This eBook will go beyond just talking about how to streamline manufacturing but also provide in-depth insights into topics that aren’t always covered to the same degree but are just as important to ...

September is Sickle Cell Awareness Month, and millions of people worldwide are living with the disease. But advances in ...

ProBio recently opened a gene therapy hub in a 128,000-square-foot facility in Mercer County, bringing more than 100 ...

A one-time experimental treatment shows unprecedented success in slowing Huntington's disease, according to UCL researchers.

Preliminary results from a small trial offer the clearest evidence yet that the brain disease’s progression can be slowed.

SynGenSys, a biotechnology company designing synthetic gene promoter systems to address critical bottlenecks in biopharma ...

Thanks to in-utero blood transfusion technology, what was once a fatal diagnosis in the womb can now result in live births. However, this medical advancement created a new challenge: a growing ...