In a study reported by Uniqure, which developed the experimental gene therapy, scientists found that it slowed progression of ...

Huntington’s disease has been successfully treated for the first time using a gene therapy, which may be available in the US as soon as next year ...

Gene therapies for rare diseases are frequently developed then discarded by drug companies because they can’t afford to ...

Scientists reported positive results on a trial for a potential Huntington's disease treatment Sept. 24, 2025. Here's what to ...

Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct ...

A company called uniQure has announced promising results from a trial of a new gene therapy for Huntington's disease. The ...

This sponsored article was provided by a partner and is not editorial content from Los Angeles Magazine or the Engine Vision Media Network. Every cell in your body holds a unique genetic code within ...

After three patients died, the maker of an investigational gene therapy stopped shipments of the drug after it refused to ...

At the European Cell & Gene Therapy Summit 2025, funding challenges and innovation drove discussions on the sector’s future.

Preliminary results from a small trial offer the clearest evidence yet that the brain disease’s progression can be slowed.

September is Sickle Cell Awareness Month, and millions of people worldwide are living with the disease. But advances in ...